Named-Patient Program

NPP-Menkes

Menkes International • Experimental Treatment Program
Elesclomol-Copper (ES-Cu) • Free of Charge

About the Program

NPP-Menkes is an experimental treatment program using Elesclomol-Copper (ES-Cu) for children with Menkes disease, completely free of charge. Launched in 2020 and coordinated by Menkes International, it operates under authorisation by AEMPS (Spain), Swissmedic (Switzerland) and the respective national medicines agencies in Germany and France.

13
Children under treatment
8
In Spain
(AEMPS authorised)
2
In Switzerland
(Swissmedic authorised)
2
In Germany
1
In France

What Menkes International Provides

API Donated

Active Pharmaceutical Ingredient (API) donated free of charge for every enrolled patient.

Clinical Advice

Scientific and clinical advice provided through the Copperless Committee.

Hospital Coordination

Coordination with hospitals for drug formulation and administration.

Family Support

Ongoing guidance and support to families throughout the treatment process.

How to Access

1
Formal request by the physician and family to MICu
2
Approval by the hospital Ethics Committee
3
Authorization by the national medicines agency

Contact & Resources

For physicians and families seeking to enrol a patient, or for more information about the program.